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Development of a Rabbit Model for Adrenoleukodystrophy: A Pilot Study on Gene Therapy Using Raav9

Xiaoya Zhou,Chui-Yan Ma,Xiaoxian Zhang, Xianchuan Xu,Fuyu Duan, Meng Kou,Hongsheng Liu, Liang Zeng,Liyan Guo, Shaoxiang Chen, Li Chen, Ziyue Li, Jie Luo,Jieying Wu, Zhejin Li,Zhanjun Li, Tingting Sui, Ping Yuan,Zhijian Lin, Hao Chen

Molecular Therapy Nucleic Acids(2025)

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