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Using a Semi-Mechanistic Model to Predict Efficacious Dosing Regimens and Optimal Drug Design Properties for a LNP-Delivered Mrna UGT1A1 Replacement Therapy in Crigler-Najjar Syndrome Type 1 Patients

Jamie Nosbisch,Marc Presler, Saheli Sarkar, David Bassen, Carter Johnson,Diana Marcantonio,Joshua Apgar,David Flowers

MOLECULAR THERAPY(2024)

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