An Optimized System for AAV Compatible Delivery of Full Length PCDH15 for Treatment of USH1F Via RNA End Joining Claire E. Williams, Ryan H. Hsu, Kip J. Hermann,Lukas C. Bachmann,Samuel L. PfaffMOLECULAR THERAPY(2024)引用 0|浏览1AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要