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DEVELOPMENT OF STANDARDIZED HUMAN-DERIVED MYELIN CONTAINING NEUROMUSCULAR ORGANOIDS AS A REFERENCE MODEL FOR CMT1A

Tamira van Wermeskerken, Bieke Bekaert, Nathan Donies,Vincent Timmerman

JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM(2024)

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关键词
Charcot-Marie-Tooth disease,neuromuscular organoids,standardization,CMT1A heterogeneity,therapeutics testing
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