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Allele-Specific Editing of a Dominant SCN8A Epilepsy Variant Protects Against Seizures and Lethality in a Murine Model

Wenxi Yu,Sophie F. Hill, Yumei Huang,Limei Zhu, Yiannos Demetriou,Julie Ziobro, Faith Reger, Xiaoyan Jia,Joanna Mattis,Miriam H. Meisler

Annals of Neurology(2024)

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