Changes in Forced Vital Capacity over ≤ 13 Years among Patients with Late-Onset Pompe Disease Treated with Alglucosidase Alfa: New Modeling of Real-World Data from the Pompe Registry.
Journal of Neurology（2024）
Key words
Forced vital capacity,Late-onset Pompe disease,Alglucosidase alfa,Observational study,Real-world evidence,Pompe Registry
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