Genetic and Functional Correction of Argininosuccinate Lyase Deficiency Using CRISPR Adenine Base Editors
AMERICAN JOURNAL OF HUMAN GENETICS（2024）
Key words
CRISPR,genome editing,ABE,lipid nanoparticles,LNP,mRNA,genetic defect,liver,argininosuccinic aciduria,ASL
AI Read Science
Must-Reading Tree
Example
Generate MRT to find the research sequence of this paper
Chat Paper
Summary is being generated by the instructions you defined