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Utilizing AAV-mediated LEAPER 2.0 for Programmable RNA Editing in Non-Human Primates and Nonsense Mutation Correction in Humanized Hurler Syndrome Mice.

Zongyi Yi,Yanxia Zhao,Zexuan Yi,Yongjian Zhang, Gangbin Tang,Xiaoxue Zhang,Huixian Tang,Wei Zhang, Ying Zhao,Huayuan Xu, Yuyang Nie, Xueqing Sun, Lijun Xing, Lian Dai,Pengfei Yuan,Wensheng Wei

GENOME BIOLOGY(2023)

引用 9|浏览33
关键词
RNA Editing,ADAR Deaminases,RNA Phase Transitions,Gene Editing,Multiplex Genome Editing
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