A Randomized, Placebo-Controlled Phase 3 Trial of the PI3Kδ Inhibitor Leniolisib for Activated PI3Kδ Syndrome
V. Koneti Rao,Sharon Webster,Anna Šedivá,Alessandro Plebani,Catharina Schuetz,Anna Shcherbina,Niall Conlon,Tanya Coulter,Virgil A. Dalm,Antonino Trizzino,Yulia Zharankova,Elaine Kulm,Julia Körholz,Vassilios Lougaris,Yulia Rodina,Kath Radford,Jason Bradt,Klaus Kucher,Anurag Relan,Steven M. Holland Blood(2023)
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