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Absence of Lenadogene Nolparvovec DNA in a Brain Tumor Biopsy from a Patient in the REVERSE Clinical Study, a Case Report

BMC Neurology(2022)

引用 5|浏览13
关键词
Case report,Viral vector transduction,Recombinant adeno-associated virus vector 2 serotype 2,ND4,qPCR assay,Lenadogene nolparvovec,Leber hereditary optic neuropathy
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