Nusinersen in Later-Onset Spinalmuscular Atrophy Long-term Results from the Phase 1/2 Studies
Basil T. Darras,Claudia A. Chiriboga,Susan T. Iannaccone,Kathryn J. Swoboda,Jacqueline Montes,Laurence Mignon,Shuting Xia,C. Frank Bennett,Kathie M. Bishop,Jeremy M. Shefner,Allison M. Green,Peng Sun,Ishir Bhan,Sarah Gheuens,Eugene Schneider,Wildon Farwell,Darryl C. De Vivo,Diana Castro, Margaret Cowie,Heather Gilbreath,Shanda Johnson, Melissa Kauk, Muna Khan, Ebra McElroy, Erin Neil Kneirbein,Leslie Nelson, Lauren Smith, Stephanie Trest, Sonya Aziz-Zaman,Joshua Cappell,Andrei Constantinescu,Rosangel Cruz,Jahannaz Dastgir,Sally Dunaway,Nicole Holuba,Alexander G. Khandji,Samantha Kramer,Jonathan Marra, Courtney Ortiz-Miller, Molly Popolizio,Rachel Salazar, Luz Sanabria,Douglas M. Sproule,Louis Weimer,Charles Berde, Ibrahim Binalsheikh, Robert Graham,Peter Kang,Anjali Koka, Mary Landrigan-,Wendy Liew,Jennifer Markowitz, Michael Paldino,Sanjay Prabhu,Navil Sethna,Edward Yang,Russell Butterfield,Deanna DiBella,Melissa Dixon, Summer Gibson, Erin Howard, Breanna Jensen, Nicholas E. Johnson, Donna Lei,Katie Mayne,Kelley J. Murphy, Tara Marie Newcomb, Suyi Niu, Michelle Page,Evan Pucillo, Chris Ramos, Aarati Rao, Nicole M. Rausch, Winter C. Redd, Sandra Reyna Villanueva, James Rian Davis, Ai Sakonji,Abby L. Smart,Susan Sorenson, Austin Stevens,Rachel Tennyson, Donata V. Trussell, Janine L. Wood, Michael J. Workman
NEUROLOGY(2019)
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